The European decision on Scholar Rock’s SMA treatment apitegromab will depend on upcoming FDA results from a U.S. plant ...

Serving as her friend Andrea's maid of honor enabled columnist Connie Chandler to reciprocate the kind of care Andrea always ...

After several excruciating months of hip pain, columnist Brianna Albers finally has not only an answer — arthritis — but a treatment plan.

England is expanding newborn screening to identify babies before SMA symptoms appear and support earlier treatment.

It's uncomfortable when people stare at her medical equipment, but columnist Alyssa Silva has learned to flip the script.

SMA patients with scoliosis show abnormal spinal muscle metabolism. These metabolic flaws lead to cellular energy deficiency ...

After 5 years on oral treatment Evrysdi, 90% of children with SMA type 1 were alive, and many reached motor milestones, a ...

Muscle ultrasound helps assess muscle health and its association with motor function in SMA children treated with Spinraza, a study reports.

One of the queerest ways to spend Pride Month could go like this … You decide to go to the theater one night. You scan the ticketing site for a show and land on one about lesbian identity, struggles, ...

The latest understandings in SMA disease type, severity, and progression. Plus, how to make an accurate diagnosis and ...

Itvisma, a one-time gene therapy for SMA, is now EU-approved for patients ages 2 and older. The expanded approval in Europe gives gene therapy access to older children, teens, and adults with SMA, ...