The novel treatment, partly developed by CHOP, eliminates the need for regular infusions while preventing the life-threatening bleeds caused by the condition.

Novo Nordisk has a factor VIII mimetic in a phase 3 trial, and a Chinese company is forging ahead with its gene therapy ...

When Brianna gave birth to her son Domenic, she never expected to hear the words “hemophilia B.” With no family history of ...

The antibiotic, effective against resistant respiratory infections, represents a historic leap in India’s pursuit of ...

In a 13-year follow-up by St. Jude Children’s Research Hospital and University College London published today in The New England Journal of Medicine, Andrew Davidoff, MD, St. Jude Department of ...

While recent advances in gene therapy have offered unprecedented options for patients with hemophilia, new data presented at ...

LITTLE ROCK — Medical researchers in Britain have successfully treated six patients suffering from the blood-clotting disease known as hemophilia B by injecting them with the correct form of a ...

“Beyond UniQure, the pipeline includes highly promising approaches that will ideally move the goal from merely managing ...

December 13, 2011 — Transfer of the factor IX gene into hepatocytes via peripheral vein infusion is effective against hemophilia B, report Amit C. Nathwani, MD, PhD, from University College London, ...

Regeneron Pharmaceuticals ((REGN)) announced an update on their ongoing clinical study. Take advantage of TipRanks Premium at 50% off! Unlock powerful investing tools, advanced data, and expert ...

Just before the Covid-19 pandemic, it seemed gene therapies were a few years away from curing all sorts of diseases with a quick, simple infusion. The idea was that drugmakers could stuff some genetic ...